September 06, 2015 – The American Food and Drug Administration just approved Uridine Triacetate (Xuriden), the first FDA-approved treatment for patients with hereditary orotic aciduria. Hereditary orotic aciduria is a rare metabolic disorder, which has been reported in approximately 20 …

Uridine Triacetate (Xuriden), a new orphan drug approved to treat rare autosomal recessive disorder Read more »