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Home › Posts tagged Exon 51

Tag: Exon 51

Eteplirsen (Exondys 51) for Duchenne Muscular Dystrophy (DMD) approved

By Joseph Gut - thasso Posted on September 20, 2016 Posted in Genetic Background, In The Press, New Drug Approval, Personalized Medicine, Pharmacogenetics, Rare Diseases, Regulatory Approval, Targeted Therapy, Thasso Post, Theragenomic Medicine 1 Comment Tagged with American Food & Drug Administration (FDA), Duchenne Muscular Dystrophy (DMD), Dystrophin Gene, Eteplirsen (Exondys 51), Exon 51, Mutation, Targeted Therapy, Thasso Post, Theragenomic Medicine

Eteplirsen (Exondys 51) for Duchenne Muscular Dystrophy (DMD) approved

September 19, 2016 – This post presents below a virtually unedited announcement by the American Food & Drug Administration (FDA) concerning Duchenne Muscular Dystrophy (DMD) therapy option which gives much hope for at least some of the affected patients. However, be …

Eteplirsen (Exondys 51) for Duchenne Muscular Dystrophy (DMD) approved Read more »

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