November 25, 2023 – Sickle cell anemia  is an inherited disease of red blood cells (erythrocytes). It belongs to the group of hemoglobinopathies (hemoglobin disorders) and leads to corpuscular hemolytic anemia. Affected people have a mutation in the hemoglobin β …

Sickle cell anemia: Genetic scissors drug approved for first time Read more »

September 16, 2022 – Beta thalassemias (β thalassemias) are a group of inherited blood disorders. They are forms of thalassemia caused by reduced or absent synthesis of the beta chains of hemoglobin that result in variable outcomes ranging from severe anemia …

Gene therapy: Hope for patients with beta-thalassemia? Read more »